Genetic diseases

Stem cells to cure type 1 diabetes

Transplantation of stem cells islets cures patient from type 1 diabetes

2024 Nobel prize laurates in medicine or physiology

Nobel prize in medicine awarded to microRNA discoverers

Hemophilia A treatment with recombinant clotting factor.

Recombinant drug coagulation factor with extended half-life prevents bleeding in children with severe hemophilia A

Antisense therapy fails to delay the progression of Huntignton’s disease